Research spotlight: Study provides a window into public perceptions about technological treatment options for brain conditions
Peer-Reviewed Publication
Updates every hour. Last Updated: 12-Sep-2025 19:11 ET (12-Sep-2025 23:11 GMT/UTC)
Some patients with a rare form of ALS benefited from an experimental therapy, with biomarker evidence of reduced injury to neurons and even limited functional recovery.
A collaborative team of researchers led by vision scientists from the School of Veterinary Medicine at the University of Pennsylvania have developed new tools to improve gene therapy in advanced stages of inherited retinal diseases (IRDs) such as retinitis pigmentosa and Leber congenital amaurosis. “This study addresses one of the biggest hurdles in IRD treatment: how to deliver effective gene therapy after a large portion of the retina has already degenerated,” says Raghavi Sudharsan of Penn Vet.